Orphan Drug Success: Engaging Key Stakeholders to Deliver Positive Outcomes
Rare diseases afflict as many as 30 million Americans, nearly 10% of the US population. Realizing the revenue potential of orphan drugs, midsize and large pharmaceutical companies increased their investment in the market. The orphan drug marketplace represents a significant opportunity for research-based biopharmaceutical firms. This white paper describes the opportunities and challenges in marketing orphan drugs and gives an overview of the stakeholders in the marketplace.